Guest writer Steve Way wants to share the things he wishes people had said to him following his diagnosis of muscular ...
Increasing pain and weakness are making it more and more challenging for columnist Robin Stemple to move his body, especially ...
Columnist Shalom Lim discusses a new independent film in which all of the disabled characters were played by actors with ...
Rayna Haque reflects on her brother Anjar's life with LGMD, including his passion for wrestling, and his legacy of love and ...
For DJ Kevin Kaelin, who lives with Duchenne muscular dystrophy, the power of music lets the crowd see beyond his physical ...
As columnist Betty Vertin prepares to move into a new house, she finds the most relaxing to do is go to DMD clinic visits with her sons.
Scientists can now explain why treatment with one steroid slows growth in young boys with Duchenne MD, while use of a newer one doesn't.
Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Print Preferred Source on Google The U.S. Food and Drug Administration (FDA) has granted both fast ...
Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit I recently traveled with my family from Carrollton, Georgia, to the PPMD conference in Orlando, ...
Epicrispr Biotechnologies has raised $90 million in financing to support late-stage clinical testing of EPI-321, the company’s epigenetic treatment candidate for facioscapulohumeral muscular dystrophy ...
The U.S. Food and Drug Administration (FDA) has allowed the enrollment of up to 30 additional boys with Duchenne muscular dystrophy (DMD) in a clinical study testing an experimental stem cell therapy.
The University of Alabama at Birmingham (UAB) has launched an expanded access program to make the experimental exon-skipping therapy delpacibart zotadirsen (del-zota) available to qualifying patients ...